Genomic and Biologic Therapies for ADRD (U01 Clinical Trial Optional)
This grant supports translating genome editing and other biologic therapies for Alzheimer's Disease-Related Dementias across the full translational pipeline. It funds work such as therapeutic lead optimization, drug product development, IND-enabling studies, early clinical evaluation, safety pharmacology, toxicology, scalable manufacturing, and formulation aligned with regulatory expectations.
Key facts
Update history