Reissue of RFA-FD-22-001 - Efficient and Innovative Natural History Studies Addressing Unmet Needs in Rare Diseases (R01 Clinical Trials Optional)

This grant supports efficient and innovative natural history studies that provide high-quality, interpretable data to address critical knowledge gaps in rare diseases. It funds work that advances medical product development and removes barriers to progress for a specific rare disease or multiple diseases with similar pathophysiology.